Quantitative Systems Pharmacology-Based Digital Twins Approach Supplements Clinical Trial Data for Enzyme Replacement Therapies in Pompe Disease Publication Quantitative Systems Pharmacology-Based Digital Twins Approach Supplements Clinical Trial Data for Enzyme Replacement Therapies in Pompe Disease Pompe disease is a rare and complex condition with severe infantile-onset (IOPD) and late-onset (LOPD)…CertaraDecember 4, 2024