Gene Therapy: A Transformative Shift in Rare Disease Treatment Video Gene Therapy: A Transformative Shift in Rare Disease Treatment After decades of promise, gene therapy is finally starting to deliver on its potential—especially for…CertaraFebruary 26, 2025
2025 cell and gene challenges: Scalability, supply chain and manufacturing Press Coverage 2025 cell and gene challenges: Scalability, supply chain and manufacturing Explore insights on 2025 challenges in cell and gene therapy, including commercial viability, with expert…CertaraFebruary 3, 2025
CMS Cell and Gene Therapy (CGT) Access Model Explained: The Most Significant Drug Pricing Legislation You’ve Never Heard Of Blog CMS Cell and Gene Therapy (CGT) Access Model Explained: The Most Significant Drug Pricing Legislation You’ve Never Heard Of December 13, 2024 The Centers for Medicare & Medicaid Services (CMS) is piloting a program…CertaraDecember 13, 2024
Model-Informed Approaches and Innovative Clinical Trial Design for Adeno-Associated Viral Vector-Based Gene Therapy Product Development: A White Paper Publication Model-Informed Approaches and Innovative Clinical Trial Design for Adeno-Associated Viral Vector-Based Gene Therapy Product Development: A White Paper The promise of viral vector-based gene therapy (GT) as a transformative paradigm for treating severely…CertaraJune 14, 2023
The Promises and Pitfalls of Gene Therapy for Rare Diseases On-Demand Webinar The Promises and Pitfalls of Gene Therapy for Rare Diseases The state of gene therapy faces much uncertainty as recent regulatory and clinical setbacks have…CertaraApril 29, 2021
Getting Gene Therapies to Patients Blog Getting Gene Therapies to Patients This blog discusses the challenges that drug developers face in getting patients access to cell…CertaraFebruary 16, 2021
Early Value Assessment in Gene Therapy Clinical Trial Design Case Study Early Value Assessment in Gene Therapy Clinical Trial Design A global biotechnology company engineering precision genetic medicine for rare diseases was in need of…CertaraFebruary 12, 2021
Dose Optimization using the Gene Therapy Virtual Twin Platform Blog Dose Optimization using the Gene Therapy Virtual Twin Platform This blog explains how using the Gene Therapy Virtual Twin™ Platform can help optimize dosing…CertaraJanuary 22, 2021